Lynch DR, Goldsberry A, Rummey C, Farmer J, Boesch S, Delatycki MB, Giunti P, Hoyle JC, Mariotti C, Mathews KD, Nachbauer W, Perlman S, Subramony SH, Wilmot G, Zesiewicz T, Weissfeld L, Meyer C. Ann Clin Transl Neurol.2024 Jan;11(1):4-16.

Date de publication : Janvier 2024

Article : Propensity matched comparison of omaveloxolone treatment to Friedreich ataxia natural history data – PubMed (nih.gov)